North Star Assessment for limb-girdle type muscular dystrophies (NSAD)
North Star Assessment for limb-girdle type muscular dystrophies (NSAD)
Download scientific diagram | North Star Assessment for limb-girdle type muscular dystrophies (NSAD) person-item threshold distribution plot demonstrating good coverage of items for the population. The top histogram illustrates the abilities of the population, from the weakest on the left to the strongest on the right. The bottom histogram demonstrates a well-distributed range of items that test the ability of the population, with a ceiling for the individuals who were the very strongest and asymptomatic. from publication: Validation of the North Star Assessment for Limb-Girdle Type Muscular Dystrophies | Objective. The North Star Assessment for limb-girdle type muscular dystrophies (NSAD), a clinician-reported outcome measure (ClinRO) of motor performance, was initially developed and validated for use in dysferlinopathy, an autosomal recessive form of limb-girdle muscular | Muscular Dystrophy, Limb-Girdle Muscular Dystrophies and Neuromuscular Diseases | ResearchGate, the professional network for scientists.
PDF) North Star Ambulatory Assessment, 6-minute walk test and timed items in ambulant boys with Duchenne muscular dystrophy
More limb girdle case reports give Sarepta some solace
SEC Filing Sarepta Therapeutics, Inc.
NSAD Psychometric Evaluation Summary Using Rasch Mathematical Methods a
SEC Filing Sarepta Therapeutics, Inc.
North Star Ambulatory Assessment - Physiopedia
An Open Label Exploratory Clinical Trial Evaluating Safety and Tolerability of Once-Weekly Prednisone in Becker and Limb-Girdle Muscular Dystrophy - IOS Press
PDF] Assessment of disease progression in dysferlinopathy
PDF] Assessment of disease progression in dysferlinopathy